Duchenne muscular dystophy: A short review and treatment update
Iranian Journal of Child Neurology,
Vol. 15 No. 2 (2021),
1 Esfand 2021
https://doi.org/10.22037/ijcn.v16i1.33282
Abstract
After advances in clinical care and newer efforts in therapeutic approaches, life span has lengthened in Duchenne muscular dystrophy (DMD). Starting from eary 1980s, each decade lead to a five year gain. DMD is not simply a monogenic X-linked disorder, it is a multisystemic condition. Pulmonary, cardiac, endocrine, gastrointestinal, and bone health aspects need careful monitoring along with pyschology, physiotherapy, social and family as a whole.
Molecular treatments are becoming facts, which some are already at hand. Some others are expected to be available within the next two years.
- Duchenne muscular dystrophy; Clinical care; Newer treatments
How to Cite
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