SEDIGHI, Parinaz; AFSHIN FAYYAZI; FIROZEH HOSSEINI; KIANA KARIMI; HOSSEIN ESFAHANI; SEYYED MOHAMMAD MAHDI HOSSEINY. From Genes to Function: Clinical Experience with the Effectiveness and Safety of Risdiplam and Nusinersen in Spinal Muscular Atrophy. Iranian Journal of Child Neurology, [S. l.], v. 20, n. 3, p. 55–61, 2026. DOI: 10.22037/ijcn.v20i3.51971. Disponível em: https://journals.sbmu.ac.ir/ijcn/article/view/51971. Acesso em: 27 jul. 2026.